Document Detail


The first missense alteration in the MCPH1 gene causes autosomal recessive microcephaly with an extremely mild cellular and clinical phenotype.
MedLine Citation:
PMID:  16211557     Owner:  NLM     Status:  MEDLINE    
Abstract/OtherAbstract:
Autosomal recessive primary microcephaly (MCPH) is a rare neurodevelopmental disorder characterized by mental retardation and congenital microcephaly with a head circumference at least 4 SD below age and sex means, in the absence of other significant malformations or neurological deficits. Truncating alterations in the MCPH1 gene have previously been shown to exhibit a distinct cellular phenotype, with a high proportion of prophase-like cells (>10%) due to premature chromosome condensation in early G2- and delayed decondensation in early G1-phase of the cell cycle. We report here the first patient with a homozygous substitution of a highly conserved threonine residue by an arginine (c.80C>G, Thr27Arg) localized in the N-terminal BRCT domain of MCPH1. The cellular and clinical phenotype of this patient is much less pronounced than that of previously described patients with truncating alterations in the MCPH1 gene. Firstly, the fraction of prophase-like cells accounts for just 3-4% of the cell population. Secondly, clinically, he has only a very mild mental retardation with predominantly delayed motor skills but normal verbal IQ attainment. Additionally, head circumference was less severely affected, being -2.4 SD at birth and -3 SD at the age of six years. This justifies reconsideration and widening of the clinical phenotype definition of MCPH1.
Authors:
Marc Trimborn; Reyk Richter; Nadine Sternberg; Ioannis Gavvovidis; Detlev Schindler; Andrew P Jackson; Eva-Christina Prott; Karl Sperling; Gabriele Gillessen-Kaesbach; Heidemarie Neitzel
Related Documents :
1722017 - Telomere loss: mitotic clock or genetic time bomb?
20041737 - Senescing cells share common features with dedifferentiating cells.
8142017 - Assignment of two human epidermal squamous cell carcinomas cell lines to more than one ...
16461887 - Hutchinson-gilford progeria mutant lamin a primarily targets human vascular cells as de...
15329057 - Isolation and receptor profiling of ileal enterochromaffin cells.
17186707 - Decreased internalisation of erbb1 mutants in lung cancer is linked with a mechanism co...
Publication Detail:
Type:  Journal Article; Research Support, Non-U.S. Gov't    
Journal Detail:
Title:  Human mutation     Volume:  26     ISSN:  1098-1004     ISO Abbreviation:  Hum. Mutat.     Publication Date:  2005 Nov 
Date Detail:
Created Date:  2005-10-18     Completed Date:  2006-06-13     Revised Date:  2006-11-15    
Medline Journal Info:
Nlm Unique ID:  9215429     Medline TA:  Hum Mutat     Country:  United States    
Other Details:
Languages:  eng     Pagination:  496     Citation Subset:  IM    
Copyright Information:
Copyright 2005 Wiley-Liss, Inc.
Affiliation:
Institut für Humangenetik, Charité - Universitätsmedizin Berlin, Germany.
Export Citation:
APA/MLA Format     Download EndNote     Download BibTex
MeSH Terms
Descriptor/Qualifier:
Amino Acid Sequence
Cells, Cultured
Child
Chromosomes / ultrastructure
DNA Mutational Analysis
European Continental Ancestry Group / ethnology
Humans
Male
Mental Retardation / genetics
Microcephaly / diagnosis*,  genetics*,  pathology
Molecular Sequence Data
Mutation, Missense*
Nerve Tissue Proteins / genetics*
Phenotype
Sequence Alignment
T-Lymphocytes / pathology
Chemical
Reg. No./Substance:
0/MCPH1 protein, human; 0/Nerve Tissue Proteins

From MEDLINE®/PubMed®, a database of the U.S. National Library of Medicine


Previous Document:  Nine mutations including three novel mutations among Russian patients with acute intermittent porphy...
Next Document:  Novel mutations of the PCSK9 gene cause variable phenotype of autosomal dominant hypercholesterolemi...