Document Detail


A first case of congenital TTP on the African continent due to a new homozygous mutation in the catalytic domain of ADAMTS13.
MedLine Citation:
PMID:  18443791     Owner:  NLM     Status:  MEDLINE    
Abstract/OtherAbstract:
Hereditary thrombotic thrombocytopenic purpura (TTP) is a rare disorder characterized by occlusive microvascular thrombosis, consumptive thrombocytopenia, and microangiopathic hemolytic anemia. Homozygous or compound heterozygous mutations in the ADAMTS13 gene result in a congenital severe ADAMTS13 deficiency and subsequent accumulation of ultra-large von Willebrand factor multimers, which tend to form platelet thrombi in the microcirculation. We report a first case of congenital TTP on the African continent with a new, homozygous mutation in the metalloprotease domain of ADAMTS13. An initially oligo-symptomatic presentation was followed by acute exacerbation with ischemic stroke and acute renal failure highlighting the severity of this syndrome.
Authors:
Sara C Meyer; Ramzi Jeddi; Balkis Meddeb; Emna Gouider; Bernhard Lämmle; Johanna A Kremer Hovinga
Publication Detail:
Type:  Case Reports; Journal Article; Research Support, Non-U.S. Gov't     Date:  2008-04-29
Journal Detail:
Title:  Annals of hematology     Volume:  87     ISSN:  1432-0584     ISO Abbreviation:  Ann. Hematol.     Publication Date:  2008 Aug 
Date Detail:
Created Date:  2008-06-27     Completed Date:  2008-10-30     Revised Date:  -    
Medline Journal Info:
Nlm Unique ID:  9107334     Medline TA:  Ann Hematol     Country:  Germany    
Other Details:
Languages:  eng     Pagination:  663-6     Citation Subset:  IM    
Affiliation:
Department of Hematology and Central Hematology Laboratory, Inselspital, Bern University Hospital and University of Bern, Bern, Switzerland.
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MeSH Terms
Descriptor/Qualifier:
ADAM Proteins / deficiency,  genetics*
Adolescent
Consanguinity
Humans
Male
Mutation / genetics
Plasma
Purpura, Thrombotic Thrombocytopenic / genetics*,  therapy
Tunisia
Chemical
Reg. No./Substance:
EC 3.4.24.-/ADAM Proteins; EC 3.4.24.-/ADAMTS13 protein, human

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