Document Detail


Metabolic studies in a patient with severe carnitine palmitoyltransferase type II deficiency.
MedLine Citation:
PMID:  9657346     Owner:  NLM     Status:  MEDLINE    
Abstract/OtherAbstract:
Here we report on a patient with severe ("non-classic") carnitine palmitoyltransferase type II (CPT II) deficiency. Hypoglycemia prompted by an infectious episode and associated with non-ketotic dicarboxylic aciduria orientated diagnosis towards beta-oxidation deficiency disorders. Blood carnitine levels revealed a secondary carnitine deficiency that was responsive to oral L-carnitine supplementation. Blood acylcarnitine profiles were abnormal and included acetyl (C2:0), butyryl/isobutyryl (C4:0), isovaleryl/2-methylbutyryl (C5:0), hexanoyl (C6:0), myristoyl (C14:0), palmitoyl (C16:0), hexadecenoyl (C16:1), oleyl (C18:1) and stearoyl (C18:0) carnitine. In urine, excess excretion of dicarboxylylcarnitines, mainly dodecanedioylcarnitine, was noticed. Upon carnitine supplementation, C8 to C12 fatty acylcarnitines, with decanoylcarnitine as well as C10 to C14 dicarboxylylcarnitines being prominent, were observed in urine. Biochemical measurements disclosed a severe reduction of mitochondrial CPT II activity (7% of normal values). Correlations of metabolic findings in the patient and physiological roles of CPT II are briefly discussed.
Authors:
M Fontaine; G Briand; C Largillière; P Degand; P Divry; C Vianey-Saban; B Mousson; J Vamecq
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Publication Detail:
Type:  Case Reports; Journal Article; Research Support, Non-U.S. Gov't    
Journal Detail:
Title:  Clinica chimica acta; international journal of clinical chemistry     Volume:  273     ISSN:  0009-8981     ISO Abbreviation:  Clin. Chim. Acta     Publication Date:  1998 May 
Date Detail:
Created Date:  1998-09-15     Completed Date:  1998-09-15     Revised Date:  2006-11-15    
Medline Journal Info:
Nlm Unique ID:  1302422     Medline TA:  Clin Chim Acta     Country:  NETHERLANDS    
Other Details:
Languages:  eng     Pagination:  161-70     Citation Subset:  IM    
Affiliation:
Laboratoire de Biochimie, Hôpital Huriez, Centre Hospitalier Régional-Universitaire de Lille, France.
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MeSH Terms
Descriptor/Qualifier:
Carnitine / blood,  urine
Carnitine O-Palmitoyltransferase / deficiency*
Cells, Cultured
Female
Fibroblasts / enzymology
Humans
Infant
Chemical
Reg. No./Substance:
541-15-1/Carnitine; EC 2.3.1.21/Carnitine O-Palmitoyltransferase

From MEDLINE®/PubMed®, a database of the U.S. National Library of Medicine


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