Document Detail


MECP2 abnormality phenotypes: clinicopathologic area with broad variability.
MedLine Citation:
PMID:  16225826     Owner:  NLM     Status:  MEDLINE    
Abstract/OtherAbstract:
Rett syndrome is a neurodevelopmental disorder that occurs worldwide and predominantly affects girls. The MECP2 gene has been put forward as the underlying gene. Interestingly, other clinical presentations in addition to Rett syndrome have been reported to be the results of deviations in MECP2. This prompted us to outline a working hypothesis of how these diverse phenotypes are connected. Our aim was to summarize the clinical picture of deviations in MECP2 at this moment to obtain a comprehensive overview. Thus, we have attempted to create a gradient, starting at the left with the most severely affected MECP2-deviant subgroups, represented by boys who are diseased in the intrauterine phase or as neonates, and at the right, the most mildly affected subgroup, female asymptomatic carriers. In the center, with dominant numbers, we have placed classic Rett syndrome presentations, together with the late-onset Rett syndrome variant and preserved speech variant. In conclusion, we feel that it is important to emphasize that Rett syndrome is a strictly clinical diagnosis that is not identical to the far broader concept of MECP2 deviations.
Authors:
Anna Erlandson; Bengt Hagberg
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Publication Detail:
Type:  Journal Article; Review    
Journal Detail:
Title:  Journal of child neurology     Volume:  20     ISSN:  0883-0738     ISO Abbreviation:  J. Child Neurol.     Publication Date:  2005 Sep 
Date Detail:
Created Date:  2005-10-17     Completed Date:  2005-12-06     Revised Date:  -    
Medline Journal Info:
Nlm Unique ID:  8606714     Medline TA:  J Child Neurol     Country:  Canada    
Other Details:
Languages:  eng     Pagination:  727-32     Citation Subset:  IM    
Affiliation:
Department of Clinical Genetics, Göteborg University Sahlgrenska University Hospital, Sweden. anna.erlandson@clingen.gu.se
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MeSH Terms
Descriptor/Qualifier:
Angelman Syndrome / genetics,  pathology
Autistic Disorder / genetics,  pathology
Female
Heterozygote
Humans
Male
Mental Retardation / genetics,  pathology
Microcephaly / genetics,  pathology
Mutation / genetics*
Phenotype*
Rett Syndrome / genetics,  pathology

From MEDLINE®/PubMed®, a database of the U.S. National Library of Medicine


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