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Histone deacetylase inhibitor suberoylanilide hydroxamic acid normalizes the levels of very long chain fatty acids in human skin fibroblasts from X-Adrenoleukodystrophy patients and downregulates the expression of proinflammatory cytokines in Abcd1/2 silenced mouse astrocytes.
MedLine Citation:
PMID:  21891797     Owner:  NLM     Status:  Publisher    
Abstract/OtherAbstract:
X-Adrenoleukodystrophy (X-ALD) is a peroxisomal metabolic disorder, caused by mutations in the ABCD1 gene encoding the peroxisomal ABC transporter adrenoleukodystrophy protein (ALDP). The consistent metabolic abnormality in all forms of X-ALD is an inherited defect in the peroxisomal β-oxidation of very long chain fatty acids (VLCFA>C22:0) and the resultant pathognomic accumulation of VLCFA. The accumulation of VLCFA leads to a neuroinflammatory disease process associated with demyelination of the cerebral white matter. The present study underlines the importance of a potent histone deacetylase (HDAC) inhibitor suberoylanilide hydroxamic acid (SAHA) in inducing the expression of ABCD2 (ALDRP), and normalizing the peroxisomal β-oxidation as well as the saturated and monounsaturated VLCFAs in cultured human skin fibroblasts of X-ALD patients. The expression of ELOVL1, the single elongase catalysing the synthesis of both saturated VLCFA (C26:0) and mono-unsaturated VLCFA (C26:1), was also reduced by SAHA treatment. In addition, using Abcd1/Abcd2-silenced mouse primary astrocytes we examined the effects of SAHA in VLCFA-induced inflammatory response. SAHA treatment decreased the inflammatory response as expression of inducible nitric oxide synthase, inflammatory cytokine, and activation of NF-κB in Abcd1/Abcd2-silenced mouse primary astrocytes was reduced. These observations indicate that SAHA corrects both the metabolic disease of VLCFA as well as the secondary inflammatory disease; therefore, it may be an ideal drug candidate to be tested for X-ALD therapy in humans.
Authors:
Jaspreet Singh; Mushfiqqudin Khan; Inderjit Singh
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Publication Detail:
Type:  JOURNAL ARTICLE     Date:  2011-9-4
Journal Detail:
Title:  Journal of lipid research     Volume:  -     ISSN:  0022-2275     ISO Abbreviation:  -     Publication Date:  2011 Sep 
Date Detail:
Created Date:  2011-9-5     Completed Date:  -     Revised Date:  -    
Medline Journal Info:
Nlm Unique ID:  0376606     Medline TA:  J Lipid Res     Country:  -    
Other Details:
Languages:  ENG     Pagination:  -     Citation Subset:  -    
Affiliation:
Medical University of South Carolina, United States;
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