Document Detail


Enhanced target gene knockdown by a bifunctional shRNA: a novel approach of RNA interference.
MedLine Citation:
PMID:  20596090     Owner:  NLM     Status:  MEDLINE    
Abstract/OtherAbstract:
RNA interference (RNAi) is a natural cellular regulatory process that inhibits gene expression by transcriptional, post-transcriptional and translational mechanisms. Synthetic approaches that emulate this process (small interfering RNA (siRNA), short hairpin RNA (shRNA)) have been shown to be similarly effective in this regard. We developed a novel 'bifunctional' RNAi strategy, which further optimizes target gene knockdown outcome. A bifunctional construct (bi-sh-STMN1) was generated against Stathmin1, a critical tubulin modulator that is overexpressed in human cancers. The bifunctional construct is postulated to concurrently repress the translation of the target mRNA (cleavage-independent, mRNA sequestration and degradation) and degrade (through RNase H-like cleavage) post-transcriptional mRNA through cleavage-dependent activities. Bi-sh-STMN1 showed enhanced potency and durability in parallel comparisons with conventional shRNA and siRNAs targeting the same sequence. Enhanced STMN1 protein knockdown by bi-sh-STMN1 was accompanied by target site cleavage at the mRNA level showed by the rapid amplification of complementary DNA ends (RACE) assay. Bi-sh-STMN1 also showed knockdown kinetics at the mRNA level consistent with its multieffector silencing mechanisms. The bifunctional shRNA is a highly effective and advantageous approach mediating RNAi at concentrations significantly lower than conventional shRNA or siRNA. These results support further evaluations.
Authors:
D D Rao; P B Maples; N Senzer; P Kumar; Z Wang; B O Pappen; Y Yu; C Haddock; C Jay; A P Phadke; S Chen; J Kuhn; D Dylewski; S Scott; D Monsma; C Webb; A Tong; D Shanahan; J Nemunaitis
Publication Detail:
Type:  Journal Article; Research Support, Non-U.S. Gov't     Date:  2010-07-02
Journal Detail:
Title:  Cancer gene therapy     Volume:  17     ISSN:  1476-5500     ISO Abbreviation:  Cancer Gene Ther.     Publication Date:  2010 Nov 
Date Detail:
Created Date:  2010-10-18     Completed Date:  2011-01-27     Revised Date:  -    
Medline Journal Info:
Nlm Unique ID:  9432230     Medline TA:  Cancer Gene Ther     Country:  England    
Other Details:
Languages:  eng     Pagination:  780-91     Citation Subset:  IM    
Affiliation:
Gradalis, Inc., Dallas, TX, USA.
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MeSH Terms
Descriptor/Qualifier:
Base Sequence
Cell Line, Tumor
Gene Knockdown Techniques / methods*
Genetic Vectors
Humans
Molecular Sequence Data
RNA Interference*
RNA, Messenger / metabolism
RNA, Small Interfering / metabolism*
Stathmin / genetics,  metabolism*
Transcription, Genetic
Chemical
Reg. No./Substance:
0/RNA, Messenger; 0/RNA, Small Interfering; 0/STMN1 protein, human; 0/Stathmin

From MEDLINE®/PubMed®, a database of the U.S. National Library of Medicine


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