Document Detail


Drug delivery trends in clinical trials and translational medicine: challenges and opportunities in the delivery of nucleic acid-based therapeutics.
MedLine Citation:
PMID:  20575003     Owner:  NLM     Status:  MEDLINE    
Abstract/OtherAbstract:
The ability to deliver nucleic acids (e.g., plasmid DNA, antisense oligonucleotides, siRNA) offers the potential to develop potent vaccines and novel therapeutics. However, nucleic acid-based therapeutics are still in their early stages as a new category of biologics. The efficacy of nucleic acids requires that these molecules be delivered to the interior of the target cell, which greatly complicates delivery strategies and compromises efficiency. Due to the safety concerns of viral vectors, synthetic vectors such as liposomes and polymers are preferred for the delivery of nucleic acid-based therapeutics. Yet, delivery efficiencies of synthetic vectors in the clinic are still too low to obtain therapeutic levels of gene expression. In this review, we focus on some key issues in the field of nucleic acid delivery such as PEGylation, encapsulation and targeted delivery and provide some perspectives for consideration in the development of improved synthetic vectors.
Authors:
Long Xu; Thomas Anchordoquy
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Publication Detail:
Type:  Journal Article; Research Support, N.I.H., Extramural; Review    
Journal Detail:
Title:  Journal of pharmaceutical sciences     Volume:  100     ISSN:  1520-6017     ISO Abbreviation:  J Pharm Sci     Publication Date:  2011 Jan 
Date Detail:
Created Date:  2010-12-16     Completed Date:  2011-03-31     Revised Date:  2011-09-22    
Medline Journal Info:
Nlm Unique ID:  2985195R     Medline TA:  J Pharm Sci     Country:  United States    
Other Details:
Languages:  eng     Pagination:  38-52     Citation Subset:  IM    
Copyright Information:
2010 Wiley-Liss, Inc. and the American Pharmacists Association
Affiliation:
Department of Pharmaceutical Sciences, University of Colorado, 12700 East Nineteenth Avenue, Aurora, Colorado 80045, USA.
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MeSH Terms
Descriptor/Qualifier:
Animals
Biological Therapy / trends*
Chemistry, Pharmaceutical
Drug Delivery Systems / trends*
Humans
Nucleic Acids / administration & dosage*,  therapeutic use*
Oligonucleotides / administration & dosage,  therapeutic use
Oligonucleotides, Antisense / administration & dosage,  therapeutic use
Plasmids / administration & dosage,  therapeutic use
RNA, Small Interfering / administration & dosage,  therapeutic use
Vaccines, DNA / administration & dosage,  therapeutic use
Grant Support
ID/Acronym/Agency:
EB005476-01A2/EB/NIBIB NIH HHS; R01 EB005476-01A2/EB/NIBIB NIH HHS
Chemical
Reg. No./Substance:
0/Nucleic Acids; 0/Oligonucleotides; 0/Oligonucleotides, Antisense; 0/RNA, Small Interfering; 0/Vaccines, DNA

From MEDLINE®/PubMed®, a database of the U.S. National Library of Medicine


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