Document Detail


Anophthalmia-esophageal atresia syndrome caused by an SOX2 gene deletion in monozygotic twin brothers with markedly discordant phenotypes.
MedLine Citation:
PMID:  16892407     Owner:  NLM     Status:  MEDLINE    
Abstract/OtherAbstract:
The clinical combination of anophthalmia/microphthalmia and esophageal atresia was first recognized in 1988 as a distinct variable multi-system malformation syndrome and since then at least 17 cases of the disease have been described, all of them sporadic in occurrence. We report a heterozygous SOX2 gene mutation underlying the syndrome of anophthalmia/microphthalmia-esophageal atresia and demonstrate that this entity can be associated to considerable clinical variability as shown by the discordant ocular phenotype observed in monozygotic twin brothers carrying an SOX2 deletion. This is the first report describing a strikingly discordant eye phenotype in monozygotic twins with the condition, with one of our patients being the first reported individual carrying an SOX2 lesion associated with unilateral eye defect. We discuss the probable sources for this remarkable phenotypic heterogeneity of the anophthalmia/microphthalmia syndrome in individuals with an identical genetic constitution.
Authors:
Juan Carlos Zenteno; Hector J Perez-Cano; Monica Aguinaga
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Publication Detail:
Type:  Case Reports; Journal Article; Research Support, Non-U.S. Gov't; Twin Study    
Journal Detail:
Title:  American journal of medical genetics. Part A     Volume:  140     ISSN:  1552-4825     ISO Abbreviation:  Am. J. Med. Genet. A     Publication Date:  2006 Sep 
Date Detail:
Created Date:  2006-08-24     Completed Date:  2006-10-24     Revised Date:  2008-11-21    
Medline Journal Info:
Nlm Unique ID:  101235741     Medline TA:  Am J Med Genet A     Country:  United States    
Other Details:
Languages:  eng     Pagination:  1899-903     Citation Subset:  IM    
Affiliation:
Department of Genetics, Institute of Ophthalmology "Conde de Valenciana," Mexico City, Mexico. jczenteno@salud.gob.mx
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MeSH Terms
Descriptor/Qualifier:
Anophthalmos / diagnosis*,  genetics*
Esophageal Atresia / diagnosis*,  genetics*
Gene Deletion
HMGB Proteins / genetics*
Humans
Infant
Male
Phenotype
SOXB1 Transcription Factors
Syndrome
Transcription Factors / genetics*
Twins, Monozygotic
Chemical
Reg. No./Substance:
0/HMGB Proteins; 0/SOX2 protein, human; 0/SOXB1 Transcription Factors; 0/Transcription Factors

From MEDLINE®/PubMed®, a database of the U.S. National Library of Medicine


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